Dr. Alessandra Biffi Telethon Institute for Gene Therapy, Italy

Alessandra Biffi is the director of the Gene therapy Program at Dana-Farber/Boston Children’s Cancer and Blood Disorders Center. Her previous position was in Milano, at the San Raffaele Telethon Institute for Gene Therapy, where she trained and developed a Research and Clinical Unit dedicated to the treatment of lysosomal storage... read moredisorders (LSDs) by means of hematopoietic stem cell (HSC)-based approaches. Biffi is actively involved in gene therapy trials for genetic diseases of childhood. Her specific research is dedicated at enhancing the efficacy of HSC-based therapeutic approaches for LSDs with severe nervous system involvement.